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Alexion launches ‘colourUp4RARE challenge’ to mark Rare Disease Day 2024

The campaign is aimed at raising awareness of how to improve quality of life for patients

- PMLiVE

Shortening the Journey at the Unusual Suspects Meeting

Medscape will be continuing their mission to shorten the diagnostic journey for patients with a rare disease at this year’s Unusual Suspects event on February 21.The Unusual Suspects is an...

Medscape Education Global

Rare Disease Diagnostic Odyssey

Medscape Education Global

- PMLiVE

Rare disease market access – Launching orphan drugs in secondary markets: the Nordic and MENA regions

Join us live at 1.00pm (GMT)/2.00pm (CET)/8.00am (EST) on Thursday 29th February, to explore rare disease market access challenges and learn more about these high potential markets.

Mtech Access

- PMLiVE

We Can Shorten the Journey

During the shortest month of the year, Medscape Education is making a renewed commitment to use clinician education to help shorten the diagnostic and treatment journey for the millions of...

Medscape Education Global

- PMLiVE

AstraZeneca’s rare disease unit receives NICE recommendation for Wolman disease therapy in infants

The enzyme replacement therapy will become the first treatment available on the NHS for the rare genetic disease

Rare Disease Learning Center Sizzle Reel

Medscape Education Global

- PMLiVE

AstraZeneca and Cellectis enter gene therapy partnership worth over $2.2bn

The deal gives AZ access to Cellectis’ gene editing technologies and manufacturing capabilities

- PMLiVE

Impacting Lives with Rare Disease Education

Education on rare diseases is crucial. Estimates suggest there are approximately 10,000 rare diseases, with 263–446 million people affected worldwide.Since its launch in September 2022, the Medscape Pathways in Rare...

Medscape Education Global

- PMLiVE

AstraZeneca latest to sue US government over Medicare drug price negotiation plan

The programme already faces court challenges from drugmakers and industry groups

- PMLiVE

Medscape’s Rare Disease Learning Center Has Reached 1 Million Learners

The Pathways in Rare Disease Learning Center celebrates a momentous achievement - engaging one million learners in its educational initiatives. This milestone signifies a profound impact on clinician confidence in...

Medscape Education Global

- PMLiVE

AstraZeneca’s rare disease unit to acquire Pfizer’s early-stage gene therapies for $1bn

The transaction could potentially see staff associated with the portfolio move to Alexion

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