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BMN 307

This page shows the latest BMN 307 news and features for those working in and with pharma, biotech and healthcare.

FDA pauses BioMarin gene therapy trial

FDA pauses BioMarin gene therapy trial

The study for BMN 307 in genetic disease phenylketonuria will be paused while malignancies in mice are explored. ... Six of the seven animals administered BMN 307 at the highest dose group developed liver tumours, five had adenomas and one a

Latest news

  • EU nod for BioMarin’s second PKU therapy Palynziq EU nod for BioMarin’s second PKU therapy Palynziq

    The company anticipates filing an IND for its gene therapy, named BMN 307, in the second half of 2019. ... The company says BMN 307 has demonstrated lifetime normalisation of Phe in a validated PKU mouse model, results which it hopes to replicate in

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