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Cerdelga

This page shows the latest Cerdelga news and features for those working in and with pharma, biotech and healthcare.

R&D productivity takes off

R&D productivity takes off

Among these, notable examples include PTC Therapeutics' Translarna (ataluren) - the first medicine approved for the treatment of Duchenne muscular dystrophy (DMD) - and Sanofi/Genzyme's Cerdelga (eliglustat) for Gaucher disease, a

Latest news

  • Genzyme's oral Gaucher drug cleared in Europe Genzyme's oral Gaucher drug cleared in Europe

    Genzyme's oral Gaucher drug cleared in Europe. Cerdelga now available to adults with type 1 Gaucher disease. ... In contrast, Cerdelga and Zavesca are glucosylceramide synthase inhibitors, which work by reducing the substrate for the deficient enzyme.

  • Orphan drugs in latest CHMP recommendations Orphan drugs in latest CHMP recommendations

    The Committee for Medicinal Products for Human Use (CHMP) backed Genzyme's Cerdelga (eliglustat) and Boehringer Ingelheim's Ofev (nintedanib) in its latest round of opinions - which are usually followed by ... Cerdelga has demonstrated it is as effective

  • Sanofi plans 18 new product launches by 2020 Sanofi plans 18 new product launches by 2020

    The remainder of its growth portfolio are Cerdelga (eliglustat) for Gaucher disease - the only approved oral, first-line therapy for the rare genetic disease, Lemtrada (alemtuzumab) for multiple sclerosis and sarilumab,

  • FDA gives green light to Genzyme’s oral Gaucher drug FDA gives green light to Genzyme’s oral Gaucher drug

    FDA gives green light to Genzyme’ s oral Gaucher drug. Oral therapy Cerdelga is set to complement intravenous Cerezyme. ... the possibility that Cerdelga could be used alongside Cerezyme as a combination regimen.

  • Genzyme on track for eliglustat filing in 2013 Genzyme on track for eliglustat filing in 2013

    Says oral Gaucher disease drug as effective as its injectable Cerezyme

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Latest Intelligence

  • Deal Watch table for November 2014 Deal Watch table for November 2014

    Cerdelga (eliglustat) sold by Vertex. Acquisition 75% royalty stream. 66. Five Prime Therapeutics / BMS.

  • Pharma deals during November 2014 Pharma deals during November 2014

    In another similar deal, PDL Biopharma acquired the 75% of the University of Michigan's worldwide royalty interest in Cerdelga (eliglustat) for $66m. ... Cerdelga, an oral therapy for adult patients with Gaucher disease type 1, was developed by Genzyme

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