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gene-editing

This page shows the latest gene-editing news and features for those working in and with pharma, biotech and healthcare.

FDA starts speedy review of Novartis’ sickle cell antibody

FDA starts speedy review of Novartis’ sickle cell antibody

Hope of a long-term cure for the disease lies with gene therapy, and there has been encouraging progress on that front as well. ... Meanwhile, a CRISPR-based gene-editing therapy is in development at CRISPR Therapeutics and Vertex, with trials of the

Latest news

  • GSK joins forces with Doudna’s CRISPR lab GSK joins forces with Doudna’s CRISPR lab

    New recruit Chris Miller will head GSK's functional genomics push. GlaxoSmithKline’s research chief Hal Barron is deepening its investment in cutting-edge science via a new CRISPR gene-editing ... The university’s Laboratory of Genomics Research (LGR)

  • Vertex eyes Duchenne market with Exonics, CRISPR deals Vertex eyes Duchenne market with Exonics, CRISPR deals

    Biotech has gene-editing expertise. Vertex Pharma has agreed a pair of deals to build a position in gene-editing therapeutics for diseases like Duchenne muscular dystrophy. ... That deal also focuses on gene-editing technology directed at DMD and DM1.

  • Poseida gets Novartis backing for myleoma CAR-T challenger Poseida gets Novartis backing for myleoma CAR-T challenger

    Poseida’s suite of proprietary gene editing technologies include the piggyBac DNA Modification System, Cas-CLOVER and TAL-CLOVER site-specific nucleases and Footprint-Free Gene Editing. ... It is being manufactured using the firm’s Cas-CLOVER site

  • Sanofi exits R&D pact with Alnylam on rare disease Sanofi exits R&D pact with Alnylam on rare disease

    Sanofi and Alnylam started working together on gene-silencing therapies in 2014, with the French drugmaker’s rare disease unit Genzyme making a $700m investment in the RNA interference specialist and ... The French drugmaker is also working on

  • Sangamo surges on data for haemophilia A gene therapy Sangamo surges on data for haemophilia A gene therapy

    nuclease (ZFN) gene-editing platform for rare disease Hunter syndrome. ... reduces risk in the company’s other gene therapy programmes which include candidates for Fabry disease, amyotrophic lateral sclerosis and Huntington’s disease.

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Approximately 5 fully matching, plus 38 partially matching documents found.

Latest Intelligence

  • Bluebird: on a mission to ‘recode’ the DNA of healthcare Bluebird: on a mission to ‘recode’ the DNA of healthcare

    Europe is the test ground for the gene therapy pioneer’s outcomes-based model, which could set the standard for the emerging sector. ... These include pipeline gene-editing therapies from Sanofi and luspatercept from Celgene to name but a few, although

  • Vertex: a vision of treating all CF patients worldwide draws closer Vertex: a vision of treating all CF patients worldwide draws closer

    A gene therapy cure for all the world’s CF patients would be a truly remarkable achievement. ... These include alpha-1 antitrypsin deficiency and focal segmental glomerulosclerosis. It’s also working with CRISPR Therapeutics on phase 1/2 clinical

  • 2019: CRISPR and therapeutic gene editing comes of age 2019: CRISPR and therapeutic gene editing comes of age

    Can gene-editing deliver safe and effective therapeutics for patients with intractable diseases? ... Meanwhile, CRISPR isn’t the only gene-editing technology being used in human therapeutics, although its devotees claim it is the simplest, easiest and

  • Cutting through the noise: CRISPR Cutting through the noise: CRISPR

    Gene editing as a therapeutic tool has ignited an explosion of excitement within the industry over the past few years: the science fiction concept of being able to simply remove and ... With an array of such tools in play, scientists seem to be on the

  • Bluebird Bio: on the cusp of a gene therapy revolution Bluebird Bio: on the cusp of a gene therapy revolution

    That means gene products hitting that Glybera price of $1m are, for now at least, unlikely. ... CRISPR Therapeutics, one of the companies working with the exciting cutting-edge CRISPR/Cas9 gene editing technology, is looking to begin a phase I trial with

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Approximately 2 fully matching, plus 11 partially matching documents found.

Latest appointments

  • Eric Rhodes becomes CEO of ERS Genomics Eric Rhodes becomes CEO of ERS Genomics

    In these roles, Rhodes was responsible for commercialising the company's genome editing technologies as well as driving its research and development. ... Biosciences. Foy said: “With his deep understanding of the gene-editing landscape and extensive

  • Marc Becker joins CRISPR Therapeutics Marc Becker joins CRISPR Therapeutics

    He becomes chief financial officer. CRISPR Therapeutics has appointed Marc Becker as its new chief financial officer with remit to drive development of its gene-editing technology platform.

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Latest from PMHub

  • 'Fake news': battling misinformation in healthcare

    After reading this headline, it’s easy to assume that some form of gene editing has led to a cure for HIV. ... Should you read on, you would also discover that gene-editing was in no way used in this treatment.

  • Random42 Partner with MedCity for BioJapan 2018

    J. Leading UK health scientists, universities and national research institutions will provide insight into the UK life sciences sector, and their work in ageing, gene editing and artificial intelligence.

  • Training the next generation of biotech leaders

    Novel technologies, coupled with programmes designed to drive cell and gene research and development, are ushering in a new era of therapies. ... It’s such a disruptive advancement – it’s just incredible to think it has all been made feasible

  • Perspective on biotech

    The emerging technologies revolutionising the biotech industry – from immunotherapy breakthroughs to cutting-edge gene editing techniques.

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