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Orfadin
This page shows the latest Orfadin news and features for those working in and with pharma, biotech and healthcare.
Orphan drug firm Sobi opens new European base
In July the European Commission approved an oral suspension formulation of Orfadin (nitisinone), which treats the rare - and potentially fatal - genetic disease Hereditary Tyrosinaemia type-1 (HT-1). ... More recently the FDA this week began its review
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Sobi wins European approval for oral form of orphan drug Orfadin
Expandstreatment options for rare genetic disease HT-1. The European Commission has approved an oral suspension formulation of Swedish Orphan Biovitrum's (Sobi) Orfadin (nitisinone). ... An oral suspension of Orfadin for paediatric use will facilitate
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PatientsLikeMe takes aim at one of world's rarest diseases
disease. Although there is currently no cure for AKU, Swedish Orphan Biovitrum's tyrosinaemia treatment Orfadin (nitisinone) is used off-label to treat AKU and is expected to enter phase III
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