Please login to the form below

Not currently logged in
Email:
Password:

Rare disease UK

This page shows the latest Rare disease UK news and features for those working in and with pharma, biotech and healthcare.

Orchard plans IPO as gene therapy pipeline advances

Orchard plans IPO as gene therapy pipeline advances

UK biotech seeks funds for expanded rare disease portfolio. UK gene therapy specialist Orchard Therapeutics has filed registration documents for an initial public offering, just weeks after its latest $150m private ... It will also help bring forward its

Latest news

  • Will Shire agree to extend Takeda takeover talks? Will Shire agree to extend Takeda takeover talks?

    UK rules mean Shire must agree to extend deadline. Shire is mulling over Takeda’s improved £42.4bn ($60 bn) - and must decide by 5pm UK time tomorrow whether or not ... making a move for the Dublin-domiciled, UK-registered rare disease company.

  • emotive partners with Rare Disease UK for public awareness campaign emotive partners with Rare Disease UK for public awareness campaign

    Healthcare communications agency emotive has teamed up with Rare Disease UK to develop a public awareness campaign, which will be launched ahead of Rare Disease Day on 28 February. ... Partnering with emotive, Rare Disease UK hopes that the agency can

  • Amicus gets NICE green light for Fabry drug Amicus gets NICE green light for Fabry drug

    Oral therapy alternative Galafold approved for routine NHS use. The National Institute of Health and Care Excellence has given its blessing to Amicus' oral therapy for Fabry disease, a rare genetic ... disorder. The UK's cost-effectiveness regulator has

  • Pharma companies back Rare Disease Day Pharma companies back Rare Disease Day

    In the UK, Rare Disease Day 2014 is focusing on the implementation of the UK Strategy for Rare Diseases, launched last November. ... UK staff, in addition to taking part in the torch relay, will submit articles to the national Rare Disease Day supplement.

  • Rare disease strategy for the UK launched Rare disease strategy for the UK launched

    Rare disease research in the UK. Another key strand to the strategy seeks to position the UK as a world leader in research and development to improve the understanding and treatment ... field.”. The government also announced today that it would be

More from news
Approximately 1 fully matching, plus 9 partially matching documents found.

Latest Intelligence

  • Accelerating diagnosis in rare disease Accelerating diagnosis in rare disease

    Biopharmaceutical companies can drive effective partnerships and improve outcomes for all stakeholders and patients in the area of rare disease. ... Timely diagnosis in rare disease is one of the fundamental unmet needs for patients, healthcare

  • A rare talent A rare talent

    As part of his efforts in this area Sebastian chairs the Rare Disease Strategy Group with UK industry body the ABPI. ... Making sense of change. From a newly enlarged company to new premises, to - perhaps - new HTA arrangements for rare disease

  • The distressing impact of rare diseases The distressing impact of rare diseases

    The company, which has a significant stake in the area, conducted online surveys in January among more than 1, 000 US/UK rare disease patients, carers, doctors, payers, government/institution representatives ... A UK patient with mixed connective tissue

More from intelligence
Approximately 0 fully matching, plus 3 partially matching documents found.

Latest from PMHub

More from PMHub
Approximately 3 fully matching, plus 5 partially matching documents found.

Featured jobs

Subscribe to our email news alerts

PMHub

Add my company
Attigo (part of the Mednet Group)

We are socially intuitive. Attigo deliver inspiring creative healthcare communications, whilst leading the way as partner of choice for socially-conscious...

Latest intelligence

Alzheimer’s disease – is Europe prepared if a breakthrough treatment becomes available?
Healthcare leaders in the European Union should begin preparing for a breakthrough now...
The UK’s new five-year pricing agreement
Pharma has agreed to capped growth again - in exchange for uptake promises...
Digital applications are transforming the market access landscape
Organisations are leveraging new technology to implement a wider range of business models and, in essence, drive market access success by working smarter, faster and with greater economy....

Infographics