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SMA

This page shows the latest SMA news and features for those working in and with pharma, biotech and healthcare.

Pfizer abandons antibody for Duchenne

Pfizer abandons antibody for Duchenne

Biogen is however focusing initially on spinal muscular atrophy (SMA) and amyotrophic lateral sclerosis (ALS).

Latest news

  • Shock as NICE turns down Biogen’s SMA therapy Shock as NICE turns down Biogen’s SMA therapy

    Shock as NICE turns down Biogen’ s SMA therapy. UK’s cost effectiveness watchdog says the drug’s long-term benefits are unclear. ... in the UK with all other types of SMA do not have access to the drug.

  • Spinraza keeps Biogen buoyant ahead of Alzheimer’s data Spinraza keeps Biogen buoyant ahead of Alzheimer’s data

    There was some deceleration in new patients starting treatment with the drug, but Biogen maintains that expanding use in adult SMA patients as well as children will unlock a “large underserved ... Biogen chief executive Michel Vounatsos responded by

  • Novartis buys gene therapy firm AveXis for $8.7bn Novartis buys gene therapy firm AveXis for $8.7bn

    Last year, Biogen secured approval for the first drug treatment for SMA, a progressive, debilitating muscle-wasting disease that affects about 23, 500 patients worldwide. ... Only around 8% of SMA patients from a matched, historic cohort were still alive

  • NICE finally starts review of Biogen’s Spinraza for SMA NICE finally starts review of Biogen’s Spinraza for SMA

    NICE finally starts review of Biogen’ s Spinraza for SMA. Will evaluate the treatment based on its Single Technology Appraisal process. ... In trials, Spinraza has been show to improve survival in infants with SMA and reduce the chances that they go on

  • Biogen wins European spinal muscular atrophy first Biogen wins European spinal muscular atrophy first

    Biogen wins European spinal muscular atrophy first. Spinraza wins accelerated approval to treat patients with the most common form of SMA. ... mechanical ventilation procedures, and showing that its benefits extend to children with less-severe,

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Latest Intelligence

  • No incentive for a cure No incentive for a cure

    to 12-week course. And Spinraza from Biogen, the first ever disease-modifying treatment for spinal muscular atrophy (SMA), which increases the body’s ability to produce SMN protein critical to.

  • Deal Watch July 2016 Deal Watch July 2016

    In 2014 the partners expanded the agreement for CK-2127107 to include some neuromuscular indications, such as Spinal Muscular Atrophy (SMA).

  • Pharma deals during January 2013 Pharma deals during January 2013

    Repligen announced the signature of an exclusive worldwide licensing agreement with Pfizer to advance Repligen's spinal muscular atrophy (SMA) programme. ... SMA is an orphan neurodegenerative genetic disease that presents early in life.

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