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Extra stomach cancer indication for Cyramza in US

FDA backs Lilly drug in combination with paclitaxel chemotherapy

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Vertex submits Kalydeco combo for cystic fibrosis

Seeks approval in both US and Europe

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Orphan drug market to reach $176bn by 2020

New report suggests market will almost double in five years

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FDA approves Baxter drug for rare form of haemophilia

Obizur is derived from pig proteins

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Orphan drugs lead CHMP recommendations

Clinuvel's Scenesse is first drug set for European approval to treat rare intolerance to sunlight

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EMA offers orphan drug benefits for Ebola research

Incentives to encourage development of new treatments for the virus

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FDA awards $19m in rare disease grants

US regulator supports 15 orphan drug projects

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NICE backs Celgene’s Revlimid in bone marrow disorder

Recommends that drug can be used on NHS to treat myelodysplastic syndromes

Genentech’s Sunil Agarwal joins rare disease firm

He will serve as chief medical officer at Ultragenyx

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FDA approves drug for rare swelling diseases

Salix and Pharming’s Ruconest is made from the milk of genetically-modified rabbits

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Channel strategy and orphan drugs

A plan for guiding decisions about a product's distribution channel is particularly relevant for orphan drugs, rare diseases or specialty medicines

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FDA sets out framework for rare childhood diseases

Wants to encourage more trial use of biomarkers and speedier approval timelines

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