The Top Pharma List rankings are compiled from GlobalData's pharmaceutical revenue figures, which are based on prescription medicine sales, including generics drugs. They have been compiled below into an infographic of BioMarin's 2012 metabolic sales performance.
Winner: Dementia Strikes Children Too: Collaborative Campaigning for Access by Portland for BioMarin.
Sponsored by. by Portland for BioMarin. ... Dementia Strikes Children Too: Collaborative Campaigning for Access - by Portland for BioMarin.
by Portland for BioMarin. CLN2 is an ultra-rare form of childhood dementia that robs infants of their ability to walk, talk and see – ultimately the disease is fatal. ... Our client, BioMarin, produces the only treatment in the world that can stop the
6. BioMarin Pharmaceutical’s Valrox is an injectable gene therapy that corrects the genetic defect underlying haemophilia A – a genetic disorder caused by a missing or defective clotting protein called factor ... Even with a relatively low worldwide
of the response to what BioMarin is claiming is a one-shot therapy. ... The uncertainty of the durability of BioMarin’s drug has left space for other haemophilia A hopefuls from rival developers.
Influencing positive behaviours and delivering change is what drives us, using thought leadership, education, social and professional engagement and compelling,...