This page shows the latest cell and gene therapies news and features for those working in and with pharma, biotech and healthcare.
bluebird bio received two PRVs upon the FDA approvals of Zynteglo (betibeglogene autotemcel) for the treatment of beta-thalassaemia in adult and paediatric patients requiring regular red blood cell transfusions, and ... commercial launches of our two
An additional £60m will support investments in commercial-scale manufacturing made by companies, including further funding for cell and gene therapies and medical devices. ... This follows on from the success of the earlier Medicines and Diagnostics
said. The Discovery Centre will support AstraZeneca’s focus on specialised and precision medicines and foster the discovery and development of next-generation therapeutics, including nucleotide-based, gene-editing and cell ... therapies, said the
The health technology assessment body is running a consultation to make its processes “clear, transparent and predictable”. ... enough. “We are disappointed that proposals to appropriately value the long-term benefits of potentially curative
UDG Healthcare company Ashfield has launched a new network offering an end-to-end approach for the commercialisation of cell and gene therapies. ... Health. “EmerGENE is no different, and with over 1, 200 cell and gene therapy clinical trials currently
Novartis is providing support with a production site in the German city of Marburg, which is fully equipped for the production of recombinant proteins, as well as cell and gene therapies. ... Additional measures and discussions with potential partners to
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Recent data on our investigational CV product portfolio underscores our commitment to investing in therapies that slow or prevent CVDs as we strive to make significant developments towards the prevention of ... CVD. For example, we are investigating cell
It also signals fresh potential for existing drugs and new generations of cell and gene therapies to reach more patients. ... shackle the advance of innovative therapies, as well as contributing to poor health and premature deaths.
In working with oncology CAR-T therapies, the stakes for an efficient cell and gene therapy (CGT) supply chain are especially high because recipients are often in the later stages of ... Broader applicability to a range of solid tumours. One thing is
Let’s take this one step further. Cell and gene therapies are a new frontier in medicine that only pharma has the scientific and clinical know-how to bring to market, ... see wholesale change in healthcare (ASGCT, Gene, Cell, &RNA Therapy Landscape
The clock is ticking to improve access to gene and cell therapies for rare diseases. ... A complex and little-known framework that fails to address the specificities of gene and cell therapies.
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An expert in cell and gene therapies, Dr Ferrari joins emotive following 20 years in research as well as holding medical affairs and commercial roles in biopharma and diagnostics. ... It is also charged with developing HCP engagement on gene silencing
Stefano Buono and Richard Van Duyne join the biopharma. Abeona Therapeutics, a clinical stage biopharmaceutical company focused on developing cell and gene therapies, has expanded its board of directors through the ... He said: “Abeona’s ambitious
chief scientific officer, global business development and licensing, and chief scientific officer for its cell and gene therapy unit. ... and gene therapies for Novartis subsidiaries Systemix Inc.
He will head the clinical development of the company's pipeline of gene and cell therapies. ... therapies will be important to Oxford BioMedica as we continue to develop our broad pipeline of novel gene and cell therapies.”.
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In this report, we interview patients, researchers, and biopharmaceutical leaders to explore the complex landscape for the development of cell and gene therapies and share commercial recommendations from our specialist teams. ... Cell and gene therapies
There are more therapies to choose from and different kinds of treatments such as cell and gene therapies that require entirely different engagement models. ... And patients, while increasingly empowered, still struggle to meaningfully engage in
Gene therapy and advanced cell-based therapies offer patients hope and the potential to make them ‘chronically well’. ... Early experience with existing gene therapies has shown that long-term outcome monitoring can be challenging, but with the right
The imminent explosion of cell and gene therapies raises issues of affordability for all health systems, not just for low and middle income countries. ... Potential methods of payment proposed for expensive cell and gene therapies include:.
Gene therapy and advanced cell-based therapies offer patients hope and the potential to make them ‘chronically well’. ... Precision medicine with precision management and precision pricing; ensuring affordability in the cell and gene therapy era.
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Redbow Consulting Group is a specialist healthcare management consultancy specialising in business strategy and marketing...