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cerebral adrenoleukodystrophy

This page shows the latest cerebral adrenoleukodystrophy news and features for those working in and with pharma, biotech and healthcare.

bluebird bio sells second FDA priority review voucher for $95m

bluebird bio sells second FDA priority review voucher for $95m

Skysona (elivaldogene autotemcel) for the treatment of early, active cerebral adrenoleukodystrophy last year.

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