This page shows the latest Gene testing news and features for those working in and with pharma, biotech and healthcare.
Working with the Broad Institute, the three companies completed data processing and conducted single variant and gene-based association testing with nearly 4, 000 UK Biobank phenotypes.
Project will aim to discover and develop a gene therapy for sickle cell disease. ... Current gene therapies in clinical testing for SCD work by taking cells from a patient that are then altered in a laboratory and reintroduced to the patient in a process
As part of this first deal, Voyager received $69m upfront to advance gene therapy candidates into phase 1 testing, with AbbVie gaining the option to license one or more for further ... In 2019, French drugmaker Sanofi also scaled back on a gene therapy
Meanwhile, Audentes has several other candidates in development, including therapies for Pompe disease, Duchenne muscular dystrophy and myotonic dystrophy that are being prepared for clinical testing. ... It’s not the first gene therapy deal the
vector carrying gene designed to reduce levels of an overexpressed protein in Huntington’s disease. ... We are nearing the initiation of a phase 1/2 study of AMT-130, the first one-time administered AAV gene therapy to enter clinical testing for
EDIT-101 is also expected to become the of Editas’ gene-editing medicines to start clinical testing, as the company recently got approval for an Investigational New Drug (IND) application for ... EDIT-101 is designed to be delivered directly into the
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And even for allogeneic cell therapies and gene therapies, raw materials and analytical testing costs will also need to be reduced” Davies said. ... As a result, Lonza’s efforts to reduce cell and gene therapy production costs involve logistics, said
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Jennifer Helfer, Senior Director, Patient Advocacy &Engagement at Encoded Therapeutics Inc., discusses genomics-driven precision medicine, gene therapy misconceptions and fears, involving patients and caregivers in designing gene therapy trials, how
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