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gene therapies

This page shows the latest gene therapies news and features for those working in and with pharma, biotech and healthcare.

bluebird bio presents positive results for inherited blood disorder gene therapies

bluebird bio presents positive results for inherited blood disorder gene therapies

bluebird bio has announced updated results from its gene therapy programmes in sickle cell disease (SCD) and beta-thalassaemia (beta-thal). ... life. Beta-thal, another inherited blood disorder, is caused by a gene defect that impairs the ability of red

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  • LifeArc to launch rare disease centres across the UK LifeArc to launch rare disease centres across the UK

    Crombie said: “While there has been encouraging progress in the development of gene and cell therapies targeting the underlying defects causing EB, there remains a number of serious consequences of the ... We hope this funding will help unlock the

  • The five ‘innovation areas’ driving success in chronic diseases The five ‘innovation areas’ driving success in chronic diseases

    Excitingly, there are many such examples. Cell and gene therapy has opened the door to medicines with genuine curative intent, such as Roctavian for haemophilia A and CAR-T therapies such ... With potentially curative gene therapies such as Roctavian,

  • Harnessing innovation to change the future of chronic diseases in Europe Harnessing innovation to change the future of chronic diseases in Europe

    We have great therapies today that can stop and reverse many chronic diseases, but there are also incredible treatments coming. ... Coupled with novel technologies like cell and gene therapies – which can halt progression and potentially address the

  • The rise of biologics: is the sector ready for future demand? The rise of biologics: is the sector ready for future demand?

    The global biologics industry is thus witnessing steady growth, as new modalities – including antibody-drug conjugates (ADCs), bispecific proteins, and cell and gene therapies – now account for a significant one-third ... a skilled talent pool that

  • Genomic medicine: collaborating for diverse data Genomic medicine: collaborating for diverse data

    Recent developments in gene sequencing also mean that cardiovascular patients may soon have access to personalised medicine. ... Gene therapy:genome data can guide the development of gene therapies, where faulty genes causing disease are replaced or

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  • Executive Insight Healthcare Consultants promotes Philippe Coune to partner Executive Insight Healthcare Consultants promotes Philippe Coune to partner

    Coune brings extensive experience in the biopharmaceutical field to his new position, including the assessment of funding options for cell and gene therapies, as well as an in-depth background in ... launches. “In recent years, he has been instrumental

  • Health comms agency emotive hires new cell and gene therapy leader Health comms agency emotive hires new cell and gene therapy leader

    An expert in cell and gene therapies, Dr Ferrari joins emotive following 20 years in research as well as holding medical affairs and commercial roles in biopharma and diagnostics. ... The group has ongoing work in preparing for the global launch of one

  • Prevail Therapeutics adds to its board of directors Prevail Therapeutics adds to its board of directors

    Francois Nader joins the biotech. Prevail Therapeutics, a biotechnology company focused on the development of gene therapies for patients with neurodegenerative diseases, has strengthened its board of directors with the addition ... advance our pipeline

  • Abeona Therapeutics appoints new additions to board of directors Abeona Therapeutics appoints new additions to board of directors

    Stefano Buono and Richard Van Duyne join the biopharma. Abeona Therapeutics, a clinical stage biopharmaceutical company focused on developing cell and gene therapies, has expanded its board of directors through the ... He said: “Abeona’s ambitious

  • Avita Medical appoints CEO Avita Medical appoints CEO

    chief scientific officer, global business development and licensing, and chief scientific officer for its cell and gene therapy unit. ... and gene therapies for Novartis subsidiaries Systemix Inc.

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