Please login to the form below
rare disease unit
This page shows the latest rare disease unit news and features for those working in and with pharma, biotech and healthcare.
AZ’s new rare disease unit wins in Wilson disease
AstraZeneca’s new rare disease unit, formed through the $39bn purchase of Alexion Pharmaceuticals, had announced positive results from a phase 3 trial in Wilson disease. ... years. Alexion/AstraZeneca Rare Disease is focused on novel molecules and
Latest news
-
AZ’s PNH therapy Ultomiris wins EU backing to expand use for children
AstraZeneca’s rare disease unit Alexion has gained a positive recommendation from the European Medicines Agency’s (EMA) Committee for Medicinal Products for Human Use (CHMP) to expand the use of ... In July, AZ completed its acquisition of Alexion,
-
AstraZeneca clears latest hurdle for Alexion acquisition after EU clearance
AZ first announced the proposed acquisition of Alexion in December 2020 in a bid to bolster and diversify its drug portfolio with rare disease assets. ... If the proposed acquisition is cleared by the CMA, AZ will make Alexion a dedicated rare disease
-
UK’s Competition and Markets Authority to review AZ/Alexion merger
The Anglo-Swedish pharma company hopes to combine its own precision medicine expertise with Alexion’s specialist rare disease knowledge to leverage its capabilities in a number of therapy areas, including ... As part of these plans, AZ will make
-
AstraZeneca reports ‘strong’ Q1 results, forecasts accelerated growth in 2021
AZ has also excluded its proposed acquisition of Alexion Pharmaceuticals from this guidance, adding in the Q1 results that Alexion will become its rare disease unit and an ‘area of expertise’.
-
Rivals rise as safety issue mars Pfizer’s DMD gene therapy trial
Two patients had at least one year of follow-up and showed modest increases in the NorthStar Ambulatory Assessment (NSAA) scale, used to assess symptoms caused by the muscle-wasting disease. ... Pfizer adopted a cautious tone in its assessment of the data
More from news
Approximately 1 fully matching, plus 33 partially matching documents found.
Latest appointments
-
AZ appoints Alexion’s Aradhana Sarin as chief financial officer
Dunoyer will then go on to become chief executive officer of the Alexion unit and chief strategy officer of AZ. ... I’m looking forward to working with him in his new role as CEO, Alexion, the Rare Disease Unit of AstraZeneca, and to his continued
More from appointments
Approximately 0 fully matching, plus 1 partially matching documents found.
Latest from PMHub
-
Overcoming Patient Recruitment Challenges in Rare Disease Trials
Learning Objective. Patient recruitment challenges in rare disease studies. Challenges in sickle cells studies. ... Family/Patient perspective. Accelerating patient recruitment in rare disease studies. Speaker 1 - Whitney Taynton - Business Unit Head,
-
Focus on Rare Diseases
Lucid’s Rare Disease Business Unit currently works with clients in Fabry disease, Pompe disease, Gaucher disease, cystinosis and PKU. ... For further information about working with Lucid’s Rare Disease Business Unit, please call Alison on 01494
More from PMHub
Approximately 0 fully matching, plus 2 partially matching documents found.
Subscribe to our email news alerts
Featured jobs
- Principal Medical Writer/ Scientific Lead, Medcomms, £5K joining...
-
Highly competitive salary
- Exciting Medical Writer Career Opportunity for Postdoc, Medcomms
-
Highly competitive salary
- Lead Market Access Writer, £5K joining bonus, UK
-
Highly competitive salary
- Market Access Director, six figure base salary and £5K joining b...
-
Highly competitive salary
- World Health Organization releases latest set of COVID-19 guidelines
- BeiGene’s Brukinsa receives FDA approval for chronic lymphocytic leukaemia
- AstraZeneca/Daiichi Sankyo’s Enhertu approved by EC for advanced breast cancer
- Eli Lilly announces $450m investment in US manufacturing site
- Europe’s cancer community publishes new report on transforming patient care
- EU outlines measures to mitigate antibiotic shortage across Europe
- Innovative Trials comments on extra funding to increase access to clinical trials for cancer patients
- Gilead’s CAR-T cell therapy recommended by NICE for lymphoma
- JCVI recommends autumn COVID-19 vaccine booster for those at highest risk
- MIT researchers develop AI model to detect future lung cancer risk
- Merging global and local pharmacovigilance operations into a successful integrated approach
- Diversifying Healthcare AI with Federated Learning
- FDA and CDC investigate potential safety concern for Pfizer/BioNTech’s COVID-19 vaccine
- World Health Organization releases latest set of COVID-19 guidelines
- AbbVie and Eli Lilly leave UK’s voluntary drug pricing agreement
- EU to revise pharmaceuticals law amid antibiotic shortages
- European MPs call for urgent action against antimicrobial resistance
- The role of medical communications in building credibility for healthtech
PMHub
Videum Health
Videum Health is a premium video platform that offers brands innovative engagement strategies to reach targeted healthcare audiences on a...
Latest intelligence
- Virtual Steering Committee & Peer Influence Program
- In this customer story, we describe the methodology and results of our client’s ongoing Virtual Steering Committee & Peer Influence program....
- Meeting healthcare’s rising challenges
- The journey to discover novel therapies through digital innovation and ensure scientific advances achieve their potential...
- Report gives insights to address gaps in HCP engagement
- How does Pharma-HCP engagement need to evolve in today's digital landscape?...
